bluebird bio Submits BLA for Gene Therapy to Treat β-thalassemia
Novartis Acquires Gene Therapy Company to Expand Portfolio
Thermo Fisher Launches System to Scale Gene Therapy Workflows
FDA Clears IND for Neurogene’s Gene Therapy for Batten Disease
FDA Halts BioMarin’s Trial Assessing Gene Therapy in Rare Disease
NeuExcell, Spark Therapeutics to Develop Gene Therapy for HD