Thermo Fisher Scientific recently launched the integrated Gibco AAV-MAX Helper Free AAV Production System to enable scalable gene therapy workflows.
The solution aims to simplify AAV vector production...
FDA recently cleared Neurogene’s Investigational New Drug (IND) application for its CLN5 Batten disease gene therapy, NGN-101.
NGN-101 is an adeno-associated virus (AAV) gene therapy and...
FDA recently placed a clinical hold on BioMarin Pharmaceuticals Phase 1/2 trial evaluating its AAV5-phenylalanine hydroxylase (PAH) gene therapy in adults with the rare disease, phenylketonuria...
NeuExcell Therapeutics and Spark Therapeutics recently announced a gene therapy collaboration to develop a safe and effective treatment for patients with Huntington’s Disease (HD).
Under...
