The Health Union recently conducted a survey called Spinal Muscular Atrophy (SMA) in America to analyze the lives of people living with SMA in the United States. This rare chronic condition impacts...
On September 16, 2022, the FDA granted bluebird bio accelerated approval for their gene therapy technology, Skysona. This technology is meant to treat active cerebral adrenoleukodystrophy (CALD) in...
The European Hematology Association (EHA) recently released results from a clinical trial that implied the potential benefits of using CRISPR treatment to address pediatric sickle cell disease (SCD)....
An analysis of major psychiatric disorders — including depression, anxiety, and others — published in Nature Genetics found that subsets of mental health disorders can be grouped by their...
Magellan Healthcare and Concert Genetics recently collaborated to offer an innovative, end-to-end solution that delivers efficient management, improved quality, and accurate payment in genetic...
Tempus recently collaborated with the United States Department of Veterans Affairs (VA) National Precision Oncology Program (NPOP) to expand access to next-generation sequencing offerings and support...
Pfizer will open the first United States sites in the Phase 3 study evaluating its investigational mini-dystrophin gene therapy, fordadistrogene movaparvovec, in ambulatory patients with Duchenne...
In an ongoing genomic medicine study, a group of geneticists developed a six-part clinical genotype assay for the Department of Veterans Affairs. The new assay utilizes six polygenic risk scores (PRS)...
Thermo Fisher Scientific recently introduced the GMP-manufactured Gibco CTS TrueCut Cas9 Protein to help researchers meet stringent quality requirements when using genome editing...
Thermo Fisher Scientific recently launched the CE-IVD marked Ion Torrent Genexus Dx Integrated Sequencer, an automated, next-generation sequencing (NGS) platform that delivers results in one...
A major international study recently identified 75 genes associated with an increased risk of developing Alzheimer's disease, including 42 new genes not previously discovered.
The study...
A collaboration between researchers from government, academic, and private organizations, called the Telomere-to-Telomere Consortium, recently produced the first fully “gapless” human...
Mount Sinai scientists recently developed CRISPR technology to link genes to complex tumor characteristics at a scale and resolution not previously possible.
Perturb-map CRISPR technology uses a...
BioMarin Pharmaceuticals recently announced results from the Phase 3 GENEr8-1 study of valoctocogene roxaparvovec, an investigational gene therapy to treat adults with severe hemophilia...
Thermo Fisher Scientific recently introduced a new large-volume electroporation system that allows cell therapy developers to quickly move from clinical development to commercial...
Boehringer Ingelheim, the UK Cystic Fibrosis Gene Therapy Consortium (GTC), and Oxford Biomedica (OXB) will further accelerate the development of a potential new treatment option for patients with...
Inscripta recently granted a non-exclusive license to Hunterian Medicine, a gene-editing and gene therapy company, to access one of several CRISPR nucleases in its Madagascar family of nucleases...
Thermo Fisher Scientific recently launched a GMP-manufactured cell culture medium that supports the large-scale growth and culture of functional natural killer (NK) cells for cell and gene...
bluebird bio recently announced the completion of its rolling submission of its Biologics License Application to FDA for betibeglogene autotemcel (beti-cel) gene therapy in patients with...
Novartis recently acquired Arctos Medical to add a pre-clinical optogenetics-based AAV gene therapy program and Arctos’ proprietary technology to its ophthalmology portfolio.
Optogenetics has...
